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Summary of Product Revenues (Detail) - USD ($)
$ in Thousands
3 Months Ended
Mar. 31, 2021
Mar. 31, 2020
Disaggregation Of Revenue [Line Items]    
Products, net $ 124,926 $ 100,448
EXONDYS 51 [Member]    
Disaggregation Of Revenue [Line Items]    
Products, net 107,185 98,183
VYONDYS 53 [Member]    
Disaggregation Of Revenue [Line Items]    
Products, net 17,548 $ 2,265
AMONDYS 45 [Member]    
Disaggregation Of Revenue [Line Items]    
Products, net $ 193