FINANCIAL INFORMATION BY QUARTER (UNAUDITED) (Tables)

12 Months Ended

Dec. 31, 2018

	2017 for Quarter Ended
	December 31			September 30			June 30			March 31
	(in thousands)
Revenues:
Product, net	$	57,277		$	45,954		$	35,011		$	16,342
Total revenues		57,277			45,954			35,011			16,342

Cost and expenses:
Cost of sales (excluding amortization of in-licensed rights)		3,546			3,078			505			224
Research and development		44,441			34,239			58,908			29,119
Selling, general and administrative		32,221			28,176			36,069			26,216
EXONDYS 51 settlement and license charges		—			25,588			2,839			—
Amortization of in-licensed rights		216			780			29			28
Total cost and operating expenses		80,424			91,861			98,350			55,587
Operating loss		(23,147	)		(45,907	)		(63,339	)		(39,245	)
Other (loss) income:
Interest (expense) income and other, net		(2,693	)		184			184			335
Gain from sale of Priority Review Voucher		—			—			—			125,000
Total other (loss) income		(2,693	)		184			184			125,335
(Loss) income before income tax (benefit) expense		(25,840	)		(45,723	)		(63,155	)		86,090
Income tax (benefit) expense		(1,842	)		2,011			(109	)		2,000
Net (loss) income	$	(23,998	)	$	(47,734	)	$	(63,046	)	$	84,090

Net income (loss) per share:
Basic (loss) earnings per share	$	(0.37	)	$	(0.78	)	$	(1.15	)	$	1.53
Diluted (loss) earnings per share	$	(0.37	)	$	(0.78	)	$	(1.15	)	$	1.50
Weighted average number of shares of common stock used in calculating:
Basic (loss) earnings per share		64,277			61,528			54,976			54,850
Diluted (loss) earnings per share		64,277			61,258			54,976			56,012