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Significant Agreements - Additional Information (Detail) - USD ($)
1 Months Ended 3 Months Ended 9 Months Ended
Jun. 30, 2016
Apr. 30, 2013
Sep. 30, 2016
Sep. 30, 2016
Collaborative Arrangements And Noncollaborative Arrangement Transactions [Line Items]        
Up-front payment to purchase future royalties   $ 30,000,000    
Up-front payment upon execution of amendment $ 7,000,000      
Development milestone and up-front payments     $ 300,000 $ 7,300,000
Sales milestone recorded as an in-license right     1,000,000 1,000,000
Maximum [Member]        
Collaborative Arrangements And Noncollaborative Arrangement Transactions [Line Items]        
Additional payments to UWA on successful achievement $ 20,000,000 20,000,000    
EXONDYS 51 and Up to Five Additional Products [Member] | Maximum [Member]        
Collaborative Arrangements And Noncollaborative Arrangement Transactions [Line Items]        
Payments to UWA on successful achievement of certain development and sales milestones   $ 6,000,000    
EXONDYS 51 [Member]        
Collaborative Arrangements And Noncollaborative Arrangement Transactions [Line Items]        
Sales milestone recorded as an in-license right     $ 1,000,000 $ 1,000,000