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Condensed Balance Sheets (USD $)
Sep. 30, 2014
Dec. 31, 2013
Current assets:    
Cash and cash equivalents $ 49,667,984 $ 21,215,228
Available for sale securities 68,670,000 11,341,000
Accounts receivable 57,000 135,000
Prepaid expenses and other current assets 1,445,000 740,000
Total current assets 119,840,000 33,431,000
Property and equipment, net 204,894 30,366
Deferred offering costs   1,079,000
Other assets 125,000 125,000
Total assets 120,170,000 34,665,000
Current liabilities:    
Accounts payable 3,032,000 714,000
Accrued expenses 3,490,287 3,187,761
Total current liabilities 6,522,000 3,902,000
Other liabilities 34,000 8,000
Total liabilities 6,556,000 3,910,000
Redeemable convertible preferred stock; $0.00001 par value; 0 and 5,500,636 shares authorized at September 30, 2014 and December 31, 2013, respectively:    
Redeemable convertible preferred stock   157,827,000
Stockholders' equity (deficit):    
Common stock: $0.00001 par value; 175,000,000 and 14,700,000 authorized at September 30, 2014 and December 31, 2013, respectively; 20,300,243 and 1,383,345 shares issued and outstanding at September 30, 2014 and December 31, 2013, respectively      
Additional paid-in capital 204,048,000  
Treasury Stock, at cost, 2,553 shares (79,000)  
Accumulated other comprehensive loss (51,257) 0
Accumulated deficit (90,303,000) (127,072,000)
Total stockholders' equity (deficit) 113,614,000 (127,072,000)
Total liabilities, redeemable convertible preferred stock and stockholders' equity (deficit) 120,170,000 34,665,000
Series A redeemable convertible preferred stock
   
Redeemable convertible preferred stock; $0.00001 par value; 0 and 5,500,636 shares authorized at September 30, 2014 and December 31, 2013, respectively:    
Redeemable convertible preferred stock   39,367,000
Series B redeemable convertible preferred stock
   
Redeemable convertible preferred stock; $0.00001 par value; 0 and 5,500,636 shares authorized at September 30, 2014 and December 31, 2013, respectively:    
Redeemable convertible preferred stock   21,257,000
Series C redeemable convertible preferred stock
   
Redeemable convertible preferred stock; $0.00001 par value; 0 and 5,500,636 shares authorized at September 30, 2014 and December 31, 2013, respectively:    
Redeemable convertible preferred stock   $ 97,203,000