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COMMERCIALIZATION AGREEMENTS (Details) - USD ($)
1 Months Ended 12 Months Ended
Mar. 16, 2020
Sep. 30, 2020
Jul. 23, 2018
Oct. 19, 2017
Dec. 31, 2020
Dec. 31, 2019
Oct. 31, 2015
Nov. 30, 2009
Promissory note         $ 4,086,000 $ 4,301,000    
Brazil [Member]                
Percentage Of Adult Gaucher Patients Treated With alfataliglicerase         25.00%      
Pfizer [Member]                
Collaborative Arrangement Profit Share Percentage               40.00%
Debt Instrument, Face Amount             $ 4,300,000  
Promissory note   $ 4,300,000            
Payment on notes payable   $ 430,000            
Chiesi US Agreement and Chiesi Ex US Agreement [Member]                
Upfront Nonrefundable Non-Creditable Payment Receivable       $ 25,000,000.0 $ 50,000,000.0      
Payments in consideration for development services performed         45,000,000.0      
Payments in connection with performance of additional studies         21,100,000      
Recognized revenues related to non-refundable payment         3,500,000 4,500,000    
Future milestone payment         10,000,000.0 $ 10,000,000.0    
Chiesi US Agreement [Member]                
Upfront Nonrefundable Non-Creditable Payment Receivable     $ 25,000,000.0 25,000,000.0        
Additional Amounts Payable To Cover Development Costs     20,000,000.0          
Maximum Entitlement Of Development Costs To Cover Per Year     7,500,000          
Additional Amount Payable For Achievement Of Regulatory And Commercial Milestones     $ 760,000,000.0   $ 760,000,000.0      
Chiesi US Agreement [Member] | Maximum [Member]                
Payment On Net Sales Percentage     40.00%   40.00%      
Chiesi US Agreement [Member] | Minimum [Member]                
Payment On Net Sales Percentage     15.00%   15.00%      
Chiesi Ex US Agreement [Member]                
Upfront Nonrefundable Non-Creditable Payment Receivable       25,000,000.0        
Additional Amounts Payable To Cover Development Costs       25,000,000.0        
Maximum Entitlement Of Development Costs To Cover Per Year       10,000,000.0        
Additional Amount Payable For Achievement Of Regulatory And Commercial Milestones       $ 320,000,000.0 $ 320,000,000.0      
Chiesi Ex US Agreement [Member] | Maximum [Member]                
Payment On Net Sales Percentage       35.00% 35.00%      
Chiesi Ex US Agreement [Member] | Minimum [Member]                
Payment On Net Sales Percentage       15.00% 15.00%      
Kirin Holdings Company, Limited [Member]                
Non-Refundable Future Service Payment $ 1,000,000.0