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MAJOR CUSTOMERS, PARTNERSHIPS AND STRATEGIC ALLIANCES - Additional Information (Detail)
1 Months Ended 3 Months Ended 6 Months Ended 16 Months Ended 34 Months Ended
Apr. 05, 2018
USD ($)
Jun. 30, 2020
USD ($)
$ / shares
Apr. 30, 2020
USD ($)
$ / shares
shares
Mar. 31, 2020
USD ($)
$ / shares
Feb. 29, 2020
USD ($)
product_target
Dec. 31, 2019
USD ($)
Sep. 30, 2019
USD ($)
May 31, 2018
USD ($)
Dec. 31, 2017
USD ($)
milestone
May 31, 2017
USD ($)
Jan. 31, 2014
USD ($)
program
Jun. 30, 2020
USD ($)
product_target
Jun. 30, 2019
USD ($)
Jun. 30, 2020
USD ($)
milestone
product
option
Jun. 30, 2019
USD ($)
Sep. 30, 2019
USD ($)
Mar. 31, 2020
USD ($)
Feb. 28, 2020
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Maximum number of product targets replaced | product_target                       10            
Recognized portion of equity issued                         $ 18,000   $ 276,000      
Revenue reduction due to decrease in measure of proportional cumulative performance, percentage                         38.00%          
Revenues                       $ 21,553,000 $ 17,548,000 $ 34,629,000 25,619,000      
Other long-term liabilities   $ 6,055,000       $ 5,711,000           6,055,000   6,055,000        
California Institute For Regenerative Medicine Agreement                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Funds due under the agreement               $ 8,000,000.0                    
Other long-term liabilities   6,100,000       5,700,000           6,100,000   6,100,000        
California Institute For Regenerative Medicine Agreement | Research Grants                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Revenues                               $ 5,200,000    
Biogen MA, Inc.                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Revenues                       8,178,000 0 8,178,000 0      
Biogen MA, Inc. | Collaboration Agreements                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Revenues                       $ 6,744,000 0 6,744,000 0      
Biogen MA, Inc. | Collaboration and License Agreement                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Proceeds from collaborators         $ 125,000,000.0                          
Maximum milestone payment receivable         $ 2,370,000,000                          
Number of product targets | product_target         12                          
Number of product targets selected | product_target         3                          
Number of additional product targets | product_target         9                          
Target selection period         5 years                          
Percent of initial recognition                       2.00%            
Portion of contract asset recognized   4,100,000                   $ 4,100,000   4,100,000        
Collaboration Arrangement, Commission Fee, Portion Of Gross Proceeds, Value   7,000,000.0                   7,000,000.0   7,000,000.0        
Biogen MA, Inc. | Collaboration and License Agreement | Maximum                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Research period         7 years                          
Biogen MA, Inc. | Collaboration and License Agreement | Pre-approval Milestone                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Maximum milestone payment receivable         $ 925,000,000.0                          
Biogen MA, Inc. | Collaboration and License Agreement | Sales-based Milestone                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Maximum milestone payment receivable         $ 1,450,000,000                          
Biogen MA, Inc. | Stock Purchase Agreement                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Number of shares issued in transaction (in shares) | shares     24,420,157                              
Sale of stock, price per share (in dollars per share) | $ / shares     $ 9.2137                              
Consideration received on transaction     $ 225,000,000.0                              
Standstill restriction period         3 years                          
Standstill restriction, ownership threshold percentage ownership percentage                                   5.00%
Agreement restriction, percentage of shares held                                   50.00%
Voting provisions expiration period         2 years                          
Voting provisions, ownership threshold percentage                                   5.00%
Excess consideration received on transaction                           79,600,000        
Recognized portion of equity issued                       2,900,000            
Collaboration agreement, equity issued   145,400,000                   145,400,000   145,400,000        
Deferred revenue   197,800,000                   197,800,000   197,800,000        
Kite Pharma Inc                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Revenues                       7,422,000 9,060,000 14,641,000 17,372,000      
Kite Pharma Inc | Collaboration Agreements                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Revenues                       6,227,000 6,227,000 $ 12,454,000 12,386,000      
Kite Pharma Inc | Collaboration and License Agreement                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Milestone payments received $ 150,000,000.0                                  
Initial research term of agreement 6 years                                  
Number of options to extend initial research term | option                           2        
Extended research term of agreement                           1 year        
Separate upfront fee $ 10,000,000.0                                  
Collaborative arrangement estimated reimbursable service costs for new research plan             $ 3,400,000                      
Collaborative arrangement transaction price 189,300,000                                  
Revenues under agreement 150,000,000.0                                  
Collaborative arrangement estimated reimbursable service costs 39,300,000                                  
Deferred revenue   94,000,000.0       106,500,000           94,000,000.0   $ 94,000,000.0        
Kite Pharma Inc | Collaboration and License Agreement | Maximum                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Development and sales-based milestone payments to be received 3,010,000,000.00                                  
Kite Pharma Inc | Collaboration and License Agreement | Achievement of Specified Research, Clinical Development, Regulatory and First Commercial Sale Milestones                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Contingent development - and sales-based milestone payments to be received 1,260,000,000                                  
Kite Pharma Inc | Collaboration and License Agreement | Achievement of Specified Sales-based Milestones if Annual Worldwide Net Sales of Licensed Products Reach Specified Levels                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Contingent development - and sales-based milestone payments to be received $ 1,750,000,000                                  
Pfizer                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Milestone payments received                 $ 12,000,000.0                  
Collaborative arrangement transaction price                 $ 12,000,000.0                  
Revenues under agreement           25,000,000.0               1,100,000     $ 25,000,000.0  
Deferred revenue   700,000       4,000,000.0           700,000   700,000        
Contract to perform for others, cumulative compensation earned   24,800,000                   24,800,000   24,800,000        
Revenue reduction due to decrease in measure of proportional cumulative performance                         3,000,000.0          
Increase (decrease) in revenue   3,000,000.0   $ 2,400,000                            
Increase (decrease) in net loss   $ 3,000,000.0   $ (2,400,000)                            
Increase (decrease) in basic net loss per share (in dollars per share) | $ / shares   $ 0.02   $ (0.02)                            
Pfizer | Collaboration Agreements                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Revenues                       3,425,000 455,000 3,785,000 1,070,000      
Pfizer | SB-525 and Other Products                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Revenues under agreement                   $ 70,000,000.0                
Pfizer | C9ORF72                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Deferred revenue   $ 4,200,000       8,000,000.0           4,200,000   4,200,000        
Number of milestones included in transaction price | milestone                 0                  
Pfizer | Maximum | SB-525 and Other Products                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Potential amount to be funded for achievement of specified commercialized and sales milestones                   266,500,000                
Pfizer | Maximum | SB-525                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Milestone revenue receivable                   300,000,000.0                
Pfizer | Maximum | Other Products                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Milestone revenue receivable                   175,000,000.0                
Pfizer | Achievement of Specified Clinical Development Intellectual Property and Regulatory Milestones | Maximum | SB-525 and Other Products                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Development and sales-based milestone payments to be received                   208,500,000                
Pfizer | Achievement of First Commercial Sale Milestones | Maximum | SB-525 and Other Products                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Development and sales-based milestone payments to be received                   $ 475,000,000.0                
Pfizer | Achievement of Specified Preclinical Development Clinical Development and First Commercial Sale Milestones | Maximum | C9ORF72                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Development and sales-based milestone payments to be received                 $ 60,000,000.0                  
Pfizer | Achievement of Commercial Milestones | Maximum | C9ORF72                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Development and sales-based milestone payments to be received                 $ 90,000,000.0                  
Pfizer SB-525                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Collaborative arrangement transaction price                           104,000,000.0        
Research Service Fees                           $ 79,000,000.0        
Agreement termination, term                           15 years        
Revenues                       429,000 4,635,000 $ 3,612,000 1,595,000      
Pfizer SB-525 | Collaboration Agreements                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Revenues                       326,000 4,635,000 $ 2,516,000 1,595,000      
Pfizer SB-525 | SB-525 and Other Products                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Number of products approved | product                           0        
Number of milestones included in transaction price | milestone                           0        
Pfizer SB-525 | Milestone Achievement                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Revenues                       103,000 0 $ 1,096,000 0      
Pfizer SB-525 | Amended Collaboration And License Agreement                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Deferred revenue   200,000                   200,000   200,000        
Pfizer SB-525 | Amended Collaboration And License Agreement | SB-525 and Other Products                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Milestone revenue receivable   25,000,000.0                   25,000,000.0   $ 25,000,000.0        
Sanofi                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Revenues under agreement                     $ 20,000,000.0              
Number of products approved | product                           0        
Agreement termination, term                           180 days        
Increase (decrease) in revenue       $ (2,200,000)                            
Increase (decrease) in net loss       $ (2,200,000)                            
Increase (decrease) in basic net loss per share (in dollars per share) | $ / shares       $ (0.02)                            
Revenues                       1,792,000 3,059,000 $ 2,291,000 5,009,000      
Number of research programs | program                     2              
Sanofi | Collaboration Agreements                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Revenues                       380,000 901,000 (349,000) 1,654,000      
Sanofi | Milestone Achievement                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Revenues                       257,000 $ 0 (235,000) $ 0      
Sanofi | Collaboration and License Agreement                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Collaborative arrangement transaction price                     $ 93,300,000              
Revenues under agreement                     20,000,000.0              
Collaborative arrangement estimated reimbursable service costs                     59,800,000              
Deferred revenue   2,300,000       1,700,000           2,300,000   $ 2,300,000        
Number of milestones included in transaction price | milestone                           0        
Cumulative milestone achieved   7,000,000.0                   7,000,000.0   $ 7,000,000.0        
Sanofi | Collaboration and License Agreement | Maximum                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Development and sales-based milestone payments to be received                     276,300,000              
Sanofi | Collaboration and License Agreement | Milestone Two                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Milestone revenue receivable           $ 7,500,000                        
Milestone revenue reversal   100,000                   100,000   100,000        
Sanofi | Collaboration and License Agreement | Milestone Three                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Milestone revenue receivable   13,500,000                   13,500,000   13,500,000        
Sanofi | Collaboration and License Agreement | ST-40 Beta Thalassemia Phase 1 Clinical Trial Milestone                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Milestone payments received                           6,000,000.0        
Cumulative milestone achieved   5,600,000                   5,600,000   5,600,000        
Milestone revenue reversal   $ 100,000                   $ 100,000   $ 100,000        
Sanofi | Collaboration and License Agreement | Achievement Of Specified Clinical Development And Regulatory Milestones | Maximum                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Development and sales-based milestone payments to be received                     115,800,000              
Sanofi | Collaboration and License Agreement | Achievement of Specified Sales Milestones | Maximum                                    
Research and Development Arrangement, Contract to Perform for Others [Line Items]                                    
Development and sales-based milestone payments to be received                     $ 160,500,000